Rare Disease Report&reg Editorial Staff

Stay up-to-date on the latest rare disease news by reading the top 5 articles of the week.

Stay up-to-date on the latest rare disease news by reading the top 5 articles of the week.

Pauline Funchain MD, explains her research which focuses on assessing possible underlying genetic and familial factors in melanomas.

Radhakrishnan Ramchandren MD, highlights the recent US Food and Drug Administration’s (FDA) approval and advantages of ADCETRIS (brentuximab vedotin) in combination with chemotherapy for advanced stage, classic Hodgkin lymphoma.

The FDA has accepted the NDA and granted Priority Review to Firdapse for the treatment of LEMS.